Press Releases

The research is focused on the identification and validation of new or improved therapeutic approaches for nonsense mutations of cystic fibrosis (CF) Lower Merion, PA – February 1, 2023 — Emily’s Entourage (EE), an innovative 501(c)3 foundation that accelerates research for new treatments and a cure for the final 10% of people with cystic fibrosis (CF), including those with nonsense mutations, today... Read More

In her career dedicated to airway gene therapy research, Dr. Limberis was the first to demonstrate that lentiviral-based gene therapy “corrects” the CF airway defect in an animal model of the disease. Emily’s Entourage (EE), an innovative 501(c)3 foundation that accelerates research for new treatments and a cure for the final 10% of people with cystic fibrosis (CF), including those with nonsense... Read More

Presented to Dr. Taylor-Cousar for her passionate commitment to the final 10% of the cystic fibrosis community that do not benefit from lifesaving mutation-targeted therapies Lower Merion, PA — Nov. 11, 2022 — Emily’s Entourage (EE), an innovative 501(c)3 foundation that accelerates research for new treatments and a cure for the final 10% of people with cystic fibrosis (CF), including those with... Read More

Work from the lab of Jeffrey Beekman, PhD, and Sacha Spelier at the University Medical Center Utrecht will be tested in the lab of John D. Lueck, PhD, at the University of Rochester Medical Center The pre-clinical research project aims to leverage ACE-tRNA technology to produce a fully functional cystic fibrosis transmembrane conductance regulator (CFTR) protein to correct nonsense mutations of CF... Read More

The project will focus on leveraging the gene editing technology, called prime editing, to correct specific CFTR mutations in a safe and efficient manner and will explore the possibility to deliver this editing cargo through virus-like particles (VLP) Lower Merion, PA — Nov. 3, 2022 — Emily’s Entourage (EE), an innovative 501(c)3 foundation that accelerates research for new treatments and a cure... Read More

The project seeks to expand the use of phage therapy as a treatment for cystic fibrosis patients with nontuberculosis mycobacterium (NTM) infections Lower Merion, PA — Nov. 2, 2022 — Emily’s Entourage (EE), an innovative 501(c)3 foundation that accelerates research for new treatments and a cure for the final 10% of people with cystic fibrosis (CF), including those with nonsense mutations, today... Read More

The project introduces novel systems for correcting the cystic fibrosis transmembrane conductance regulator (CFTR) protein in the airways of people with nonsense mutations of CF Nov. 2, 2022 — Emily’s Entourage (EE), an innovative 501(c)3 foundation that accelerates research for new treatments and a cure for the final 10% of people with cystic fibrosis (CF), including those with nonsense mutations, today announced... Read More